Bootcamp participants and invited guests only. Final celebration, presentation of data, and networking at the Pittsburgh Center for Connected Medicine.

PGTB Keynote speaker — Dr. John Flannery, Professor of Neuroscience at UC Berkeley, will lecture on Gene Therapy for Retinal Degeneration. Followed by a meet-and-greet and light refreshments. Free and open to the public.

Explore career paths in gene therapy. This panel of speakers include Michelle Alabek, Genetic counselor, UPMC, Raymond Miller JD, Partner DLA Piper speaking on patent law, and Leah Byrne, PhD, Assistant Professor, University of Pittsburgh, and CSO, Avista Therapeutics, speaking on academia and industry. Free and open to the public.

Bootcamp students only. Jeff Boyd, Managing Partner, Healthcare & Life Sciences, Heidrick & Struggles will speak on opportunities in the gene therapy space, followed by shadowing experiences at local Pittsburgh biotech companies.

Bailey Bostelman, Director, Chapter Engagement East, Foundation Fighting Blindness, and Eric Bennardo, will speak about patient perspectives on gene therapy. Free and open to the public.

Bootcamp students only. Molly Johnson, Computational Lead, Avista Therapeutics leads a hands-on single-cell RNASeq data analysis exercise.

Dr. Henry Greely, Professor by courtesy of Genetics, Stanford School of Medicine; Director, Center for Law and the Biosciences; Director, Stanford Program in Neuroscience and Society; and Chair, Steering Committee of the Center for Biomedical Ethics. The Ethics of gene therapy and genome editing. Free and open to the public. Online only via Zoom - https://pitt.zoom.us/j/96237562519.

Bootcamp students only. Genome editing in a dish.

Speaker: Dr. José-Alain Sahel, Chair of Ophthalmology, UPMC - Optogenetics in the clinic. Free and open to the public.

Bootcamp students only. Optogenetics in action. Led by Dr. Mac Hooks, Willa Kerkhoff and Aydin Alikaya

Bootcamp students only. scRNA-Seq experiments, day 2.

Bootcamp students only. scRNA-Seq experiments, day 1.

Bootcamp students only. Simon Watkins leads a tour of the University of Pittsburgh Biological Imaging Center.

Bootcamp students only. Dissections of fixed tissues.

Guest speaker: Dr. Dan Chung, CMO of Sparing Vision - Opportunities in Gene Therapy. Followed by a lunch-and-learn panel on opportunities in gene therapy, led by Dr. Chung and Dr. Rob Lin, CEO of Avista Therapeutics. Free and open to the public.

Bootcamp students only. Demo and lecture: Miguel Betegon, AAV purification

Guest speaker: Dr. Joseph Martel, UPMC. Gene therapy clinical trials at UPMC. Lecture free and open to the public.

Bootcamp students only. AAV packaging and purification.

Bootcamp students only. 10X Genomics demo and training.

Bootcamp students only. AAV packaging and purification.

Introduction to the program. Followed by wetlab - AAV packaging and purification.